Found 10 matching trials
Home Therapy With VPRIV in Gaucher's Disease N/A The purpose of this study is to proof increasing patient satisfaction and p...
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Landeskrankenhaus Bregenz
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A Study of VPRIV in Participants With Gaucher Disease Previously Treated With Other Enzyme Replacement Therapies or Substrate Reduction Therapies N/A The main aim of this study is to describe the safety profile of velaglucera...
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University of Alberta/Medical Genetics Clinic
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Open-Label Extension Study Evaluating Long Term Safety in Patients With Type 1 Gaucher Disease Receiving DRX008A (ERT) PHASE1 Gaucher disease is a rare lysosomal storage disorder caused by the deficien...
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Shaare Zedek Medical Center
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An Open-Label Extension Study of GA-GCB ERT in Patients With Type 1 Gaucher Disease PHASE3 The purpose of this study is to evaluate the long-term safety of every othe...
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Los Angeles Medical Center
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Study of Gene-Activated® Human Glucocerebrosidase (GA-GCB) ERT Compared With Imiglucerase in Type I Gaucher Disease PHASE3 Gaucher disease is a rare lysosomal storage disorder caused by the deficien...
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Duke Children's Hospital & Health Center
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Study of the Effect of Velaglucerase Alfa (VPRIV®) on Bone-related Pathology in Treatment-naïve Participants With Type 1 Gaucher Disease PHASE4 The primary purpose of this study is to evaluate the effect of VPRIV therap...
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Cedars Sinai Medical Center
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A Study of Gene-Activated® Human Glucocerebrosidase (GA-GCB) Enzyme Replacement Therapy in Gaucher Disease PHASE3 Gaucher disease is a rare lysosomal storage disorder caused by the deficien...
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Hipolito Yrigoyen
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Study of GA-GCB Enzyme Replacement Therapy in Type 1 Gaucher Disease Patients Previously Treated With Imiglucerase PHASE2 Gaucher disease is a rare lysosomal storage disorder caused by the deficien...
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Regional Metabolic Center
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Retrospective and Prospective Observational Study of MRI Changes in Bone and Visceral Lesions of Patients With Type 1 Gaucher Disease Treated With VPRIV® (Velaglucerase Alfa) N/A This study with standardized reading MRIs, will provide for the first time ...
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A Survey to Assess Participants', Caregivers', and Nurses' Use and Understanding of Educational Material on Velaglucerase Alfa (VPRIV) Home Infusion N/A The main purpose of this survey is to determine participants', caregivers',...
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Multiple Locations
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